4th TMN mini-symposium : Innovative therapies applied to neurosciences

March 20, 2024

Strasbourg (France)


The development of therapeutic strategies targeting human neurological diseases is a major challenge that is driving major innovations in translational medical research. In this symposium, the speakers will present new therapeutic strategies for retinal and neuromuscular diseases, in particular through the use of stem cells and viruses. The symposium organizers will also welcome the director of the PCBIS platform in Strasbourg, which focuses on the identification of active compounds for therapeutic purposes.

This 4th mini-symposium is organised by the Translational Medicine and Neurogenetics Department of the IGBMC based in Illkirch-Graffenstaden (Strasbourg, France), in collaboration with Inserm, the University of Strasbourg and the CNRS. This symposium is led by Manon BOIVIN (PhD), Marianne LEMEE (PhD candidate), Charlotte Schurk (PhD candidate) and Jacqueline.


9h00 - 9h45

Dr Deniz Dalkara
Institut de la Vision, Paris, France

Early to late stage gene therapy interventions for inherited retinal degenerations


9h50 - 10h35

Dr Pascal Villa

Plateforme de Chimie Biologique Intégrative de Strasbourg (PCBIS)

Ecole Supérieure de Biotechnologie de Strasbourg (ESBS), France

Title to be confirmed


Coffee break


11h00 - 11h45

Dr Walter Habeler

I-STEM, Paris, France

Use of Human Pluripotent Stem Cells for retinal diseases


11h50 - 12h35

Dr Aurélie Goyenvalle

Université Paris Saclay, UFR Simone Veil, Versailles, France

AAV-mediated exon-skipping approaches for the treatment of Duchenne muscular dystrophy and its brain comorbidities


20th of March, 2024


1 rue laurent Fries,